Gene knock-in using specific TALE nucleases restores erythroid differentiation defect of human iPSC obtained from pyruvate kinase deficient patients

Autores: Garate, Z.; Quintana-Bustamante, O.; Crane, A. M. ; Cerrato, L.; Cerrato, L.; Orman, I.; Sevilla, J.; Maia, T. M. ; Ribeiro, L. M. ; Fusaki, N. ; Garcia-Sanchez, F.; Aguirre Ena, Xabier; Gouble, A.; Prosper Cardoso, Felipe; Bueren, J. A.; Davis, B. R. ; Segovia, J. C.